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Congenital Anemia

Showing 1 - 25 of 4,466

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Congenital Hemolytic Anemia, Sickle Cell Disease Trial run by the National Heart, Lung, and Blood Institute (NHLBI) (Peripheral

Recruiting
  • Congenital Hemolytic Anemia
  • Sickle Cell Disease
  • Peripheral blood hematopoietic progenitor cell (PBPC) transplant
  • +3 more
  • Bethesda, Maryland
    National Institutes of Health Clinical Center
Jan 25, 2023

Sickle Cell Anemia Trial run by the NHLBI (PBSC Transplant, Alemtuzumab, Sirolimus)

Active, not recruiting
  • Sickle Cell Anemia
  • PBSC Transplant
  • +4 more
  • Bethesda, Maryland
    National Institutes of Health Clinical Center, 9000 Rockville Pi
Oct 13, 2022

Perioperative Anemia, Surgery, Spinal Deformity Trial in Beijing (Ferric derisomaltose, Ferrous succinate)

Not yet recruiting
  • Perioperative Anemia
  • +3 more
  • Ferric derisomaltose
  • Ferrous succinate
  • Beijing, Beijing, China
    Peking Union Medical College Hospital
Jan 26, 2023

Squamous Cell Carcinoma in Fanconi Anemia

Recruiting
  • Fanconi Anemia
  • Inherited Bone Marrow Failure Syndrome
    • Bethesda, Maryland
      National Institutes of Health Clinical Center
    Feb 2, 2023

    Cancer in Inherited Bone Marrow Failure Syndromes

    Recruiting
    • Diamond Blackfan Anemia
    • +4 more
      • Bethesda, Maryland
      • +1 more
      Jan 24, 2023

      Pyruvate Kinase Deficiency, Pyruvate Kinase Deficiency Anemia, Anemia Trial in Worldwide

      Recruiting
      • Pyruvate Kinase Deficiency
      • +3 more
        • Boston, Massachusetts
        • +4 more
        Aug 5, 2022

        VO2max & HRQoL in Children With Sickle Cell Disease

        Completed
        • Sickle Cell
        • Children
          • Montpellier, Occitanie, France
            Pediatric and Congenital Cardiology Department, Arnaud De Villen
          Aug 16, 2023

          Severe Aplastic Anemia Who Developed High Risk Clonal Evolution

          Completed
          • Severe Aplastic Anemia
            • Bethesda, Maryland
              National Heart, Lung and Blood Institute (NHLBI)
            Apr 7, 2022

            Baby Detect : Genomic Newborn Screening

            Recruiting
            • Congenital Adrenal Hyperplasia
            • +126 more
              • Liege, Wallonia, Belgium
                CRMN, Hôpital La Citadelle
              Jan 24, 2023

              Acquired and Inherited Bone Marrow Failure Syndromes

              Recruiting
              • Severe Aplastic Anemia
              • +2 more
                • Bethesda, Maryland
                  National Institutes of Health Clinical Center
                Aug 12, 2022

                Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive, Acute Leukemia in Remission, Acute Lymphoblastic Leukemia

                Active, not recruiting
                • Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive
                • +36 more
                • Buffalo, New York
                  Roswell Park Cancer Institute
                Jan 23, 2023

                Cyanotic Congenital Heart Disease, Anemia, Cyanosis Trial in San Diego (Epoetin Alfa and Iron, Iron)

                Terminated
                • Cyanotic Congenital Heart Disease
                • +3 more
                • Epoetin Alfa and Iron
                • Iron
                • San Diego, California
                  Rady Children's Hospital
                Nov 3, 2021

                Congenital Dyserythropoietic Anemia (CDA) Trial in Cincinnati

                Recruiting
                • Congenital Dyserythropoietic Anemia (CDA)
                  • Cincinnati, Ohio
                    Cincinnati Children's Hospital Medical Center
                  Feb 11, 2021

                  Pediatric Pyruvate Kinase Deficiency, Pediatric Hemolytic Anemia Trial in Barcelona, Madrid (Mitapivat, Mitapivat-matching )

                  Recruiting
                  • Pediatric Pyruvate Kinase Deficiency
                  • Pediatric Hemolytic Anemia
                  • Barcelona, Spain
                  • +1 more
                  Aug 8, 2022

                  Acute Leukemia, Immune Deficiency Disorder, Congenital Hematological Disorder Trial in Rochester (radiation, drug, procedure)

                  Recruiting
                  • Acute Leukemia
                  • +9 more
                  • Total Body Irradiation 1200 cGy
                  • +7 more
                  • Rochester, New York
                    Wilmot Cancer Institute
                  Jun 20, 2022

                  Dehydrated Hereditary Stomatocytosis Trial in Boston (Senicapoc (synonyms: ICA-17043;

                  Recruiting
                  • Dehydrated Hereditary Stomatocytosis
                  • Senicapoc (synonyms: ICA-17043; 2,2-bis-(4-fluorophenyl)-2-phenylacetamide)
                  • Boston, Massachusetts
                    Boston Children's Hospital
                  Mar 1, 2022

                  Pediatric Pyruvate Kinase Deficiency, Pediatric Hemolytic Anemia Trial in Spain, United States (Mitapivat, Mitapivat-matching )

                  Recruiting
                  • Pediatric Pyruvate Kinase Deficiency
                  • Pediatric Hemolytic Anemia
                  • Phoenix, Arizona
                  • +3 more
                  Aug 8, 2022

                  Acquired Aplastic Anemia, Paroxysmal Nocturnal Hemoglobinuria, Inherited Bone Marrow Failure Syndromes Trial in Philadelphia

                  Recruiting
                  • Acquired Aplastic Anemia
                  • +2 more
                  • CliniMACs
                  • Philadelphia, Pennsylvania
                    Children's Hospital of Philadelphia
                  Mar 1, 2022

                  Stomatocytosis Trial in Le Kremlin Bicêtre

                  Recruiting
                  • Stomatocytosis
                    • Le Kremlin Bicêtre, France
                      AP-HP, Bicêtre Hospital, Pediatrics - Hematology - Reference cen
                    Oct 28, 2021

                    Acquired Pyruvate Kinase Deficiency In Clonal Myeloid Neoplasms

                    Not yet recruiting
                    • Pyruvate Kinase Deficiency
                    • +10 more
                    • Blood Draw
                    • Boston, Massachusetts
                      Massachusetts General Hospital
                    May 21, 2021

                    Sickle Cell Disease and Thalassemia Trial in Dallas (Donor Stem Cell Transplantation)

                    Withdrawn
                    • Sickle Cell Disease and Thalassemia
                    • Donor Stem Cell Transplantation
                    • Dallas, Texas
                      UT Southwestern Medical Center
                    Jul 22, 2021

                    Parvovirus B19 Infection in Hereditary Hemolytic Anemias

                    Active, not recruiting
                    • Parvovirus B19 Infection
                    • Supportive treatment with or without red cell transfusion/intravenous immune globulin (IVIG)
                    • Sohag, Egypt
                      , Faculty of Medicine, Sohag University
                    Mar 25, 2021

                    Bone Marrow Failure Syndrome, Congenital Amegakaryocytic Thrombocytopenia, Congenital Pure Red Cell Aplasia Trial in United

                    Recruiting
                    • Bone Marrow Failure Syndrome
                    • +6 more
                    • Los Angeles, California
                    • +23 more
                    Aug 15, 2022

                    Pyruvate Kinase Deficiency Trial in Stanford, Madrid (RP-L301)

                    Recruiting
                    • Pyruvate Kinase Deficiency
                    • RP-L301
                    • Stanford, California
                    • +2 more
                    Sep 22, 2021

                    Pyruvate Kinase Deficiency, Anemia, Hemolytic Trial in Worldwide (AG-348)

                    Completed
                    • Pyruvate Kinase Deficiency
                    • Anemia, Hemolytic
                    • Oakland, California
                    • +18 more
                    Dec 14, 2021