Congenital Anemia
Showing 1 - 25 of 4,466
Congenital Hemolytic Anemia, Sickle Cell Disease Trial run by the National Heart, Lung, and Blood Institute (NHLBI) (Peripheral
Recruiting
- Congenital Hemolytic Anemia
- Sickle Cell Disease
- Peripheral blood hematopoietic progenitor cell (PBPC) transplant
- +3 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 25, 2023
Sickle Cell Anemia Trial run by the NHLBI (PBSC Transplant, Alemtuzumab, Sirolimus)
Active, not recruiting
- Sickle Cell Anemia
- PBSC Transplant
- +4 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center, 9000 Rockville Pi
Oct 13, 2022
Perioperative Anemia, Surgery, Spinal Deformity Trial in Beijing (Ferric derisomaltose, Ferrous succinate)
Not yet recruiting
- Perioperative Anemia
- +3 more
- Ferric derisomaltose
- Ferrous succinate
-
Beijing, Beijing, ChinaPeking Union Medical College Hospital
Jan 26, 2023
Squamous Cell Carcinoma in Fanconi Anemia
Recruiting
- Fanconi Anemia
- Inherited Bone Marrow Failure Syndrome
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Feb 2, 2023
Cancer in Inherited Bone Marrow Failure Syndromes
Recruiting
- Diamond Blackfan Anemia
- +4 more
-
Bethesda, Maryland
- +1 more
Jan 24, 2023
Pyruvate Kinase Deficiency, Pyruvate Kinase Deficiency Anemia, Anemia Trial in Worldwide
Recruiting
- Pyruvate Kinase Deficiency
- +3 more
-
Boston, Massachusetts
- +4 more
Aug 5, 2022
VO2max & HRQoL in Children With Sickle Cell Disease
Completed
- Sickle Cell
- Children
-
Montpellier, Occitanie, FrancePediatric and Congenital Cardiology Department, Arnaud De Villen
Aug 16, 2023
Severe Aplastic Anemia Who Developed High Risk Clonal Evolution
Completed
- Severe Aplastic Anemia
-
Bethesda, MarylandNational Heart, Lung and Blood Institute (NHLBI)
Apr 7, 2022
Baby Detect : Genomic Newborn Screening
Recruiting
- Congenital Adrenal Hyperplasia
- +126 more
-
Liege, Wallonia, BelgiumCRMN, Hôpital La Citadelle
Jan 24, 2023
Acquired and Inherited Bone Marrow Failure Syndromes
Recruiting
- Severe Aplastic Anemia
- +2 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Aug 12, 2022
Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive, Acute Leukemia in Remission, Acute Lymphoblastic Leukemia
Active, not recruiting
- Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive
- +36 more
- Cyclophosphamide
- +4 more
-
Buffalo, New YorkRoswell Park Cancer Institute
Jan 23, 2023
Cyanotic Congenital Heart Disease, Anemia, Cyanosis Trial in San Diego (Epoetin Alfa and Iron, Iron)
Terminated
- Cyanotic Congenital Heart Disease
- +3 more
- Epoetin Alfa and Iron
- Iron
-
San Diego, CaliforniaRady Children's Hospital
Nov 3, 2021
Congenital Dyserythropoietic Anemia (CDA) Trial in Cincinnati
Recruiting
- Congenital Dyserythropoietic Anemia (CDA)
-
Cincinnati, OhioCincinnati Children's Hospital Medical Center
Feb 11, 2021
Pediatric Pyruvate Kinase Deficiency, Pediatric Hemolytic Anemia Trial in Barcelona, Madrid (Mitapivat, Mitapivat-matching )
Recruiting
- Pediatric Pyruvate Kinase Deficiency
- Pediatric Hemolytic Anemia
- Mitapivat
- Mitapivat-matching placebo
-
Barcelona, Spain
- +1 more
Aug 8, 2022
Acute Leukemia, Immune Deficiency Disorder, Congenital Hematological Disorder Trial in Rochester (radiation, drug, procedure)
Recruiting
- Acute Leukemia
- +9 more
- Total Body Irradiation 1200 cGy
- +7 more
-
Rochester, New YorkWilmot Cancer Institute
Jun 20, 2022
Dehydrated Hereditary Stomatocytosis Trial in Boston (Senicapoc (synonyms: ICA-17043;
Recruiting
- Dehydrated Hereditary Stomatocytosis
- Senicapoc (synonyms: ICA-17043; 2,2-bis-(4-fluorophenyl)-2-phenylacetamide)
-
Boston, MassachusettsBoston Children's Hospital
Mar 1, 2022
Pediatric Pyruvate Kinase Deficiency, Pediatric Hemolytic Anemia Trial in Spain, United States (Mitapivat, Mitapivat-matching )
Recruiting
- Pediatric Pyruvate Kinase Deficiency
- Pediatric Hemolytic Anemia
- Mitapivat
- Mitapivat-matching placebo
-
Phoenix, Arizona
- +3 more
Aug 8, 2022
Acquired Aplastic Anemia, Paroxysmal Nocturnal Hemoglobinuria, Inherited Bone Marrow Failure Syndromes Trial in Philadelphia
Recruiting
- Acquired Aplastic Anemia
- +2 more
- CliniMACs
-
Philadelphia, PennsylvaniaChildren's Hospital of Philadelphia
Mar 1, 2022
Stomatocytosis Trial in Le Kremlin Bicêtre
Recruiting
- Stomatocytosis
-
Le Kremlin Bicêtre, FranceAP-HP, Bicêtre Hospital, Pediatrics - Hematology - Reference cen
Oct 28, 2021
Acquired Pyruvate Kinase Deficiency In Clonal Myeloid Neoplasms
Not yet recruiting
- Pyruvate Kinase Deficiency
- +10 more
- Blood Draw
-
Boston, MassachusettsMassachusetts General Hospital
May 21, 2021
Sickle Cell Disease and Thalassemia Trial in Dallas (Donor Stem Cell Transplantation)
Withdrawn
- Sickle Cell Disease and Thalassemia
- Donor Stem Cell Transplantation
-
Dallas, TexasUT Southwestern Medical Center
Jul 22, 2021
Parvovirus B19 Infection in Hereditary Hemolytic Anemias
Active, not recruiting
- Parvovirus B19 Infection
- Supportive treatment with or without red cell transfusion/intravenous immune globulin (IVIG)
-
Sohag, Egypt, Faculty of Medicine, Sohag University
Mar 25, 2021
Bone Marrow Failure Syndrome, Congenital Amegakaryocytic Thrombocytopenia, Congenital Pure Red Cell Aplasia Trial in United
Recruiting
- Bone Marrow Failure Syndrome
- +6 more
- Treosulfan
- +7 more
-
Los Angeles, California
- +23 more
Aug 15, 2022
Pyruvate Kinase Deficiency Trial in Stanford, Madrid (RP-L301)
Recruiting
- Pyruvate Kinase Deficiency
- RP-L301
-
Stanford, California
- +2 more
Sep 22, 2021
Pyruvate Kinase Deficiency, Anemia, Hemolytic Trial in Worldwide (AG-348)
Completed
- Pyruvate Kinase Deficiency
- Anemia, Hemolytic
-
Oakland, California
- +18 more
Dec 14, 2021